Researchers have long dreamed of treating diseases from hemophilia to cancer by replacing mutant genes with normal ones. 研究人员长期以来一直梦想用正常基因取代突变基因的方法治疗血友病,癌症等各种疾病。
In human trials of the hemophilia treatment, patients show a response at first, but it fades over time. 在治疗血友病的人体试验中,病人最初有一些反应,但经过一段时间,这种反应就消失了。